Preclinical Safety and Efficacy of Human CD34+ Cells Transduced With Lentiviral Vector for the Treatment of Wiskott-Aldrich Syndrome
Molecular Therapy advance online publication, February 28, 2012.
doi:10.1038/mt.2012.23
Authors: Samantha Scaramuzza, Luca Biasco, Anna Ripamonti, Maria C Castiello, Mariana Loperfido, Elena Draghici, Raisa J Hernandez, Fabrizio Benedicenti, Marina Radrizzani, Monica Salomoni, Marco Ranzani, Cynthia C Bartholomae, Elisa Vicenzi, Andrea Finocchi, Robbert Bredius, Marita Bosticardo, Manfred Schmidt, Christof von Kalle, Eugenio Montini, Alessandra Biffi, Maria G Roncarolo, Luigi Naldini, Anna Villa
& Alessandro Aiuti
| Authors: |
|
Samantha Scaramuzza, Luca Biasco, Anna Ripamonti, Maria C Castiello, Mariana Loperfido, Elena Draghici, Raisa J Hernandez, Fabrizio Benedicenti, Marina Radrizzani, Monica Salomoni, Marco Ranzani, Cynthia C Bartholomae, Elisa Vicenzi, Andrea Finocchi, Robbert Bredius, Marita Bosticardo, Manfred Schmidt, Christof von Kalle, Eugenio Montini, Alessandra Biffi, Maria G Roncarolo, Luigi Naldini, Anna Villa, Alessandro Aiuti |
| Journal: |
|
Molecular Therapy
|
| Year: |
|
2012 |
| DOI: |
|
10.1038/mt.2012.23 |
| Publication date: |
|
28-02-2012 |